QRX-411 is part of ProQR's ophthalmology pipeline that currently CEO of ProQR, "The severe genetic retinal diseases we are targeting do 

2021-03-24

QR-1123 Aurora phase 1/2 study for adRP; Sepofarsen ILLUMINATE phase 2/3 study for LCA10; QR-421a STELLAR phase 1/2 study for Usher syndrome; Sepofarsen INSIGHT – phase 1b/2 study for LCA10; Sepofarsen ProQR has programs in multiple therapeutic areas, such as cystic fibrosis and the rare skin condition Dystrophic epidermolysis bullosa, but ophthalmology assets make up the bulk of its pipeline. 2021-01-07 LEIDEN, Netherlands, Nov. 30, 2015 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing lives through the creation of transformative RNA medicines for the treatment of severe orphan diseases such as cystic fibrosis (CF) and Leber's congenital amaurosis (LCA), today presents an update on the innovation pipeline and announces an R&D day for investors. 2021-03-25 2018-02-12 Agenda Overview and introduction by Daniel de Boer The relevance of the Nasal Potential Difference test in CF by JP Clancy, M.D. Results of the QR-010 NPD study by Noreen Henig, M.D. Pipeline and path ahead by Daniel de Boer Q&A session with JP Clancy, M.D., Noreen Henig, M.D., Smital Shah and Daniel de Boer ProQR Therapeutics 2 ProQR plans to independently advance its pipeline of RNA medicines to establish a multi-product, platform company in IRD. By 2023, the company expects its pipeline to have at least two commercial products, and at least three late-stage and seven early-stage programs in development. We are ProQR. About us; Vision 2023; Leadership; Careers; Contact; Science & Pipeline. Research and development pipeline; Clinical Trials.

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The company was founded by Daniel de Boer, Gerard Platenburg, Henri Termeer,  Apr 20, 2021 ProQR Therapeutics is dedicated to changing lives through the creation of we are growing our pipeline with patients and loved ones in mind. Since then, ProQR have announced that the U.S. Food and Drug Their research and development pipeline includes programmes focusing on specific forms of  ProQR Therapeutics was founded in May 2012 in Leiden, the Netherlands with the goal of ProQR's current pipeline consists of programs in cystic fibrosis,  Apr 20, 2021 Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with patients and loved ones in mind. Learn more  Mar 12, 2018 ProQR's first program, now the most advanced in its pipeline, is an RNA oligonucleotide that targets the cystic fibrosis gene CFTR. ProQR Therapeutics N.V. (Nasdaq:PRQR), a company dedicated to changing RNA repair platform technologies we are growing our pipeline with patients and  6 days ago ProQR Therapeutics is dedicated to changing lives through the creation of we are growing our pipeline with patients and loved ones in mind. News. ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher  Shehla Shakoor.

Based on its unique proprietary RNA repair platform technologies, ProQR Therapeutics is growing its pipeline with patients and loved ones in mind.

2021-04-15 · ProQR Therapeutics NV is a biopharmaceutical company, which engages in the discovery and development of RNA therapies for the treatment of severe genetic rare diseases such as Leber congenital amaurosis 10, Usher syndrome and retinitis pigmentosa. Its product pipeline include Sepofarsen, QR-421a, QR-1123, and QR-504a. In an interview with PharmaShots, Daniel A. de Boer of ProQR shared his views on P-II/III pivotal trial of Sepofarsen to treat the root cause of a rare eye disease, Leber congenital amaurosis 10 (LCA10) Shots: The Illuminate P-II/III trial of sepofarsen is a double-masked, randomized, controlled, multiple-dose study to evaluate if sepofarsen is effective […] LEIDEN, Netherlands & CAMBRIDGE, Mass., Oct. 05, 2020 (GLOBE NEWSWIRE) -- ProQR Based on our unique proprietary RNA repair platform technologies we are growing our pipeline with QRX-411 is part of ProQR's ophthalmology pipeline that currently also includes one clinical compound, QR-110 for Leber's Congenital Amaurosis Type 10, and three preclinical programs, QRX-421 for Usher syndrome, QRX-1011 for Stargardt's disease and QRX-504 for Fuchs endothelial corneal dystrophy. ProQR Announces Positive Findings From an Interim Analysis in the Phase 1/2 trial of QR-421a for Usher Syndrome and Provides Business Update 31 March 2020 at 6:00 AM EDT QR-421a showed early and encouraging evidence of activity, with 25% of patients showing a benefit across multiple concordant outcome measures and was well tolerated with no serious adverse events Learn about our mission to help treat rare genetic diseases.

ProQR has programs in multiple therapeutic areas, such as cystic fibrosis and the rare skin condition Dystrophic epidermolysis bullosa, but ophthalmology assets make up the bulk of its pipeline.

Patient-focused drug development In order to achieve our goals, ProQR strives to integrate the patient voice into our decision-making throughout the drug development process as we believe that a patient-focused strategy is crucial to our success. ProQR is a clinical stage biotech company that discovers and develops unique RNA therapies for severe genetic disorders, specialized in retinal diseases.

The live webcast can be accessed at | April 23, 2021 31st March 2020: ProQR announce promising findings from an interim analysis in the Stellar Phase 1/2 clinical trial investigating QR-421a RNA therapy for Usher Syndrome. These results are based on data from the two patient cohorts, involving a total of 14 patients. The interim analysis results indicate the safety and efficacy of QR-421a to be appropriated in treating usher Syndrome and non 2020-07-14 2021-03-11 2021-04-03 Proqr stock got battered in 2018 because of stock offerings, I believe. they also failed to progress in the cystic fibrosis pipeline (2015?) but antisense oligotides seems more risky when taken 2021-03-08 2021-04-20 2016-03-01 Proven leader with deep worldwide ophthalmology experience, including multiple approvals globallyLEIDEN, Netherlands & CAMBRIDGE, Mass., Oct. 05, 2020 (GLOBE NEWSWIRE) -- ProQR Therapeutics N.V Key updates At ARVO ProQR will present additional positive pre-clinical proof-of-concept data for QR-110 targeting LCA 10. The company has recently received IND clearance to start clinical | January 11, 2021 ProQR plans to independently advance its pipeline of RNA medicines to establish a multi-product, platform company in IRD. By 2023, the company expects its pipeline to have at least two commercial products, and at least three late-stage and seven early-stage programs in development.
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Overview; R&D Platform; Pipeline; Products; Services ProQR Therapeutics is a Leiden, NL based biotech company  The company was founded in 2019 by EB Research partnership and ProQR Therapeutics to continue development of a pipeline of potential RNA therapies for  Its product pipeline include Sepofarsen, QR-421a, QR-1123, and QR-504a.

Learn more about our Pipeline of RNA therapies.
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News. ProQR Announces Positive Results from Clinical Trial of QR-421a in Usher 

Learn more  At ProQR we develop antisense oligonucleotides, or RNA therapies, to treat genetic diseases that are rare. We have made significant progress in advancing our broad pipeline of investigational medicines through the various stages of drug development, from early discovery to late stage clinical trials. Our platform for inherited retinal diseases Science & Pipeline RNA technology to benefit patients At ProQR science is literally at the heart of what we do. The offices at our headquarters in Leiden are centered around the laboratories where our scientists discover and test our novel RNA therapies. ProQR is a clinical stage biotech company that discovers and develops unique RNA therapies for severe genetic disorders, specialized in retinal diseases. ProQR Therapeutics - Striving to reverse blindness ProQR’s pipeline now includes two clinical programs, one preclinical program and two programs ready to enter development.